We invite you to join us at the 3rd conference of the International Rare Diseases Research Consortium (IRDiRC), which will take place February 8-9, 2017 in Paris, France at the conference center of Université Pierre et Marie Curie (UPMC) Jussieu.
In December 2015 E-rare launched the eigth E-Rare joint call (JTC 2016) for funding multilateral research projects on rare diseases on “Clinical research for new therapeutic uses of already existing molecules (repurposing) in rare diseases”. Fifteen countries joined this call: Austria, Belgium, Canada (including Québec), France, Germany, Hungary, Israel, Italy, Latvia, Poland, Portugal, Romania, Spain, Switzerland, and Turkey.
The aim of the call was to enable scientists in different countries to build an effective collaboration on a common interdisciplinary research project based on complementarities and sharing of expertise, with a clear translational research approach.
The process included a two-step submission and evaluation procedure.
In the first step a total of 30 eligible proposals were submitted. After careful examination by the Scientific Evaluation Committee (SEC), 20 proposals were selected for the second stage of evaluation. Each of the full proposals have been evaluated by at least two SEC members and two additional external experts during the first stage of evaluation and the reviews were sent to project coordinators in order to give them the opportunity of studying the assessments and commenting on experts' arguments and evaluations for the second stage of evaluation. Each of the full proposals and the answer to the reviews have been evaluated by at least three SEC members for the second stage of evaluation.
Following the second SEC evaluation and ranking of the best projects, 8 consortia with a foreseen budget of about 11.2 Mio € were selected for funding.
Selected projects: DPem Title: Dimethylfumarate for the treatment of bullous pemphigoid Coordinator: Ralf Ludwig
HCQ4Surfdefect Title: Hydroxychloroquine (HCQ) in pediatric ILD Coordinator: Matthias Griese
NICOFA Title: Nicotinamide for the treatment of Friedreich ataxia Coordinator: Jörg Schulz
REALS Title: Repurposed Enoxacin for the treatment of patients with Amyotrophic Lateral Sclerosis Coordinator: Eran Hornstein
ReDox Title: Repurposing doxycycline in the treatment of AL amyloidosis Coordinator: Giovanni Palladini
ROCK-ALS Title: Inhibition of Rho Kinase (ROCK) with Fasudil as disease-modifying treatment for ALS Coordinator: Paul Lingor
ROPROP Title: Propranolol for preemptive treatment of threshold retinopathy of prematurity Coordinator: Christoph Bührer
TAMDMD Title: Tamoxifen in Duchenne muscular dystrophy - a randomised placebo controlled phase 2 trial Coordinator: Dirk Fischer
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